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Myopathy clinical trials at UCSD

2 research studies open to eligible people

Showing trials for
  • A Study of the Efficacy and Safety of 24 Week Treatment With REN001 in Patients With Primary Mitochondrial Myopathy

    open to eligible people ages 18 years and up

    This is a randomized, double-blind, placebo-controlled, parallel group, multi-centre, study designed to investigate the efficacy and safety of REN001 administered once daily over a 24-week period to patients with PMM.

    La Jolla, California and other locations

  • A Study to Evaluate ASP0367 in Participants With Primary Mitochondrial Myopathy

    open to eligible people ages 18-80

    The purpose of the phase 2 portion of this study is to select a biologically-active ASP0367 dose level by pharmacokinetic (PK) and pharmacodynamic (PD) evaluation. The phase 2 portion of this study will also assess the safety and tolerability of ASP0367. The purpose of the phase 3 portion of this study is to assess the effect of ASP0367 on functional improvement relative to placebo and will also assess the safety and tolerability of ASP0367 relative to placebo. The phase 3 portion of this study will also assess the effect of ASP0367 on functional improvement and fatigue relative to placebo and will assess the effect of ASP0367 in overall participant functioning relative to placebo.

    La Jolla, California and other locations

Our lead scientists for Myopathy research studies include .

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