Clinical trials open to people under 18
(90 trials open to new patients)

• 4H Syndrome (1 open to new patients)
• Abnormalities of Erythrocyte Differentiation or Function (1 open to new patients)
• Abnormalities of Platelets (1 open to new patients)
• Acute Lymphoblastic Leukemia (1 open to new patients)
• Acute Myeloid Leukemia (1 open to new patients)
• ADLD (1 open to new patients)
• Adrenoleukodystrophy (1 open to new patients)
• Adrenomyeloneuropathy (1 open to new patients)
• Aicardi–Goutières syndrome (1 open to new patients)
• ALD Gene Mutation (1 open to new patients)
• Alexander Disease (1 open to new patients)
• Alexanders Leukodystrophy (1 open to new patients)
• Allan-Herndon-Dudley Syndrome (1 open to new patients)
• Alopecia (2 open to new patients)
• ALSP (1 open to new patients)
• AMN (1 open to new patients)
• Amyotropic Lateral Sclerosis (ALS) (1 open to new patients)
• Anemia (2 open to new patients)
• Angelman Syndrome (2 open to new patients)
• Anti-NMDA Receptor Encephalitis (1 open to new patients)
• Antiretroviral Toxicity (1 open to new patients)
• Arthritis (2 open to new patients)
• Aspergillosis (1 open to new patients)
• Astrocytoma (1 open to new patients)
• Atopic Dermatitis (Eczema) (3 open to new patients)
• Attention-Deficit/Hyperactivity Disorder (2 open to new patients)
• Autism (2 open to new patients)
• Autoimmune Disease (2 open to new patients)
• Autoimmune Encephalitis (1 open to new patients)
• AxD (1 open to new patients)
• Bleeding Disorder (1 open to new patients)
• Blood Coagulation Disorder (1 open to new patients)
• Bone Marrow Transplant (1 open to new patients)
• BPAN (1 open to new patients)
• Brain Cancer (1 open to new patients)
• Brain Hypoxia (1 open to new patients)
• Brain Injury (1 open to new patients)
• Brain Tumor (1 open to new patients)
• Breast Cancer (1 open to new patients)
• Breastfed Infants of Mothers on Select DOI (1 open to new patients)
• Bronchiolitis Acute Viral (1 open to new patients)
• Bronchiolitis Obliterans (1 open to new patients)
• C. Diff (1 open to new patients)
• C.Difficile Diarrhea (1 open to new patients)
• CADASIL (1 open to new patients)
• Canavan Disease (1 open to new patients)
• Cancer, General (3 open to new patients)
• Cannabidiol (1 open to new patients)
• Carcinoma (3 open to new patients)
• Cardiac Arrest (1 open to new patients)
• Cardiomyopathy (1 open to new patients)
• Cardiotoxicity (1 open to new patients)
• Cardiovascular Disease (1 open to new patients)
• Cataracts (1 open to new patients)
• Cerebrotendinous Xanthomatoses (1 open to new patients)
• Cerebrotendinous Xanthomatosis (1 open to new patients)
• Charcot-Marie-Tooth Disease (1 open to new patients)
• Choriocarcinoma (1 open to new patients)
• Chronic Myeloid Leukemia (1 open to new patients)
• Churg-Strauss Syndrome (1 open to new patients)
• Cockayne Syndrome (1 open to new patients)
• Colitis (1 open to new patients)
• Colorectal Cancer (1 open to new patients)
• Connective Tissue Disorder (1 open to new patients)
• Constipation (1 open to new patients)
• COVID-19 (1 open to new patients)
• CPAP (1 open to new patients)
• Craniopharyngioma (1 open to new patients)
• Crohn's Disease (3 open to new patients)
• CSF1R Gene Mutation (1 open to new patients)
• CTX (1 open to new patients)
• Cystic Fibrosis (1 open to new patients)
• Danon Disease (1 open to new patients)
• Deletion and Duplication of Mitochondrial DNA (1 open to new patients)
• Diabetes (3 open to new patients)
• Diabetes Type 1 (2 open to new patients)
• Diabetes Type 2 (1 open to new patients)
• Diarrhea (1 open to new patients)
• Diarrhea Infectious (1 open to new patients)
• DIPG (1 open to new patients)
• Disorders of Metabolism (1 open to new patients)
• Early Labor (1 open to new patients)
• Endometrial Cancer (1 open to new patients)
• Eosinophilic Colitis (1 open to new patients)
• Eosinophilic Esophagitis (2 open to new patients)
• Eosinophilic Gastritis (1 open to new patients)
• Eosinophilic Gastroenteritis (1 open to new patients)
• Eosinophilic Gastrointestinal Disorders (EGIDs) (1 open to new patients)
• Epilepsy (1 open to new patients)
• Ewing Sarcoma (1 open to new patients)
• Executive Functioning (1 open to new patients)
• Extragonadal Embryonal Carcinoma (1 open to new patients)
• Factor IX Deficiency (1 open to new patients)
• Fallopian Tube Cancer (1 open to new patients)
• Female Reproductive System Neoplasm (1 open to new patients)
• Fertility Preservation (1 open to new patients)
• Fibrosis (1 open to new patients)
• GALC Deficiency (1 open to new patients)
• Gangliosidoses (1 open to new patients)
• Generalized Arterial Calcification of Infancy (1 open to new patients)
• Genital Neoplasms (1 open to new patients)
• Germ Cell Tumor (1 open to new patients)
• Glioblastoma (1 open to new patients)
• Glioma (4 open to new patients)
• Globoid Leukodystrophy (1 open to new patients)
• GM2 Gangliosidosis (1 open to new patients)
• Graft Versus Host Disease (1 open to new patients)
• Granulomatosis with Polyangiitis (1 open to new patients)
• Hair Diseases (1 open to new patients)
• HBSL (1 open to new patients)
• Head and Neck Surgery (1 open to new patients)
• Headache (2 open to new patients)
• Heart Failure (1 open to new patients)
• Hematologic Disease (1 open to new patients)
• Hematologic Malignancy (1 open to new patients)
• Hematologic Neoplasms (1 open to new patients)
• Hematopoietic Cell Transplantation (1 open to new patients)
• Hemolytic-Uremic Syndrome (1 open to new patients)
• Hemophilia (2 open to new patients)
• Hereditary Spastic Paraplegia (1 open to new patients)
• Hidradenitis Suppurativa (1 open to new patients)
• Histiocytic Disorders (1 open to new patients)
• HIV/AIDS (1 open to new patients)
• Hives (1 open to new patients)
• Hodgkin's Lymphoma (1 open to new patients)
• Hunter Syndrome (1 open to new patients)
• Hypotrichosis (1 open to new patients)
• Hypoxia (1 open to new patients)
• Hypoxic-Ischemic Encephalopathy (1 open to new patients)
• Implementation Science (1 open to new patients)
• Inflammatory Bowel Disease (4 open to new patients)
• Infusion Reactions (1 open to new patients)
• Intellectual Disability (1 open to new patients)
• Intensive Care, Neonatal (1 open to new patients)
• Intensive Care Units, Neonatal (1 open to new patients)
• Kidney Cancer (1 open to new patients)
• Krabbe Disease (1 open to new patients)
• Labrune Syndrome (1 open to new patients)
• Lactating Women on Select DOI (1 open to new patients)
• LBSL (1 open to new patients)
• LCC (1 open to new patients)
• Leukemia (1 open to new patients)
• Leukodystrophy (1 open to new patients)
• Leukoencephalopathies (1 open to new patients)
• LGI1-Antibody Encephalitis (1 open to new patients)
• Limb-Girdle Muscular Dystrophy (1 open to new patients)
• Liver Cancer (1 open to new patients)
• Liver Disease (2 open to new patients)
• Liver Transplant (1 open to new patients)
• Locally Advanced Malignant Solid Neoplasm (1 open to new patients)
• Low Birth Weight (1 open to new patients)
• Lupus (1 open to new patients)
• Lymphoma (1 open to new patients)
• MASLD (1 open to new patients)
• MECP2 Duplication Syndrome (1 open to new patients)
• Meningioma (1 open to new patients)
• Mental Disorder (2 open to new patients)
• Mental Health (1 open to new patients)
• Metachromatic Leukodystrophy (1 open to new patients)
• Migraine (2 open to new patients)
• Mitochondrial Diseases (1 open to new patients)
• Mitochondrial Disorders (1 open to new patients)
• Mitochondrial Encephalomyopathies (1 open to new patients)
• Mitochondrial Genetic Disorders (1 open to new patients)
• MLC1 (1 open to new patients)
• MLD (1 open to new patients)
• Mucopolysaccharidosis (2 open to new patients)
• Multiple Myeloma (1 open to new patients)
• Multiple Sulfatase Deficiency (1 open to new patients)
• Muscular Atrophy (2 open to new patients)
• Mutation (1 open to new patients)
• Narcolepsy (1 open to new patients)
• Neonatal Encephalopathy (2 open to new patients)
• Neonatal Hypoglycemia (1 open to new patients)
• Neonatal Respiratory Failure (1 open to new patients)
• Neoplasms (7 open to new patients)
• Neuromyelitis Optica Spectrum Disorders (1 open to new patients)
• Neuropathy (1 open to new patients)
• Non-Hodgkin Lymphoma (1 open to new patients)
• Nonalcoholic Fatty Liver Disease (1 open to new patients)
• Obesity (3 open to new patients)
• Ocular Melanoma (1 open to new patients)
• Ovarian Cancer (2 open to new patients)
• Ovarian Embryonal Carcinoma (1 open to new patients)
• Ovarian Tumor (1 open to new patients)
• Pathological Conditions, Anatomical (1 open to new patients)
• Pelizaeus-Merzbacher Disease (1 open to new patients)
• Peritoneal Cancer (1 open to new patients)
• Peroxisomal Biogenesis Disorder (1 open to new patients)
• Platelet Disorder (1 open to new patients)
• PLP1 Null Syndrome (1 open to new patients)
• Pregnancy (2 open to new patients)
• Premature Birth (2 open to new patients)
• Pseudoxanthoma Elasticum (1 open to new patients)
• Psoriasis (3 open to new patients)
• Psychotic Disorders (2 open to new patients)
• Pulmonary Invasive Fungal Infections (1 open to new patients)
• Rare Bleeding Disorder (1 open to new patients)
• Refsum Disease (1 open to new patients)
• Renal Cell Carcinoma (1 open to new patients)
• Retinitis Pigmentosa (1 open to new patients)
• Rett Syndrome (2 open to new patients)
• Rickets (1 open to new patients)
• Salla Disease (1 open to new patients)
• Sarcoma (2 open to new patients)
• School-based Interventions (1 open to new patients)
• Scoliosis (1 open to new patients)
• Seizures (1 open to new patients)
• Seminoma (1 open to new patients)
• Sialic Storage Disease (1 open to new patients)
• Sickle Cell Anemia (1 open to new patients)
• Sjögren (1 open to new patients)
• Sjögren-Larsson Syndrome (1 open to new patients)
• Sjögren Syndrome (1 open to new patients)
• Skin Cancer/Melanoma (3 open to new patients)
• Skin Diseases (1 open to new patients)
• Solid Neoplasm (1 open to new patients)
• Solid Tumor (4 open to new patients)
• Spastic Paraplegia (1 open to new patients)
• Spinal Deformity (1 open to new patients)
• Spinal Muscular Atrophy (2 open to new patients)
• Stem Cell Transplant (1 open to new patients)
• Surgery (1 open to new patients)
• Tay-Sachs Disease (1 open to new patients)
• TBCK-Related Intellectual Disability Syndrome (1 open to new patients)
• Team-effectiveness Research (1 open to new patients)
• Teratoma (1 open to new patients)
• Testicular Cancer (1 open to new patients)
• Thalassemia (1 open to new patients)
• Thrombophilia (1 open to new patients)
• Thrombosis (1 open to new patients)
• Tic Disorders (1 open to new patients)
• Tourette Syndrome (1 open to new patients)
• Traumatic Brain Injury (1 open to new patients)
• TUBB4A-Related Leukodystrophy (1 open to new patients)
• Ulcerative Colitis (2 open to new patients)
• Unresectable Malignant Solid Neoplasm (1 open to new patients)
• Van Der Knapp Disease (1 open to new patients)
• Vanishing White Matter Disease (1 open to new patients)
• Vitiligo (1 open to new patients)
• Von Willebrand Disease (1 open to new patients)
• Weight Management (3 open to new patients)
• White Matter Disease (2 open to new patients)
• Zellweger Syndrome (1 open to new patients)