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Rett Syndrome clinical trials at UCSD

1 in progress, 0 open to eligible people

Showing trials for
  • TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study)

    Sorry, not currently recruiting here

    The REVEAL Pediatric Study is a multi-center, Phase 1/2 open-label, dose-escalation and dose-expansion study of TSHA-102, an investigational gene therapy, in pediatric females with Rett Syndrome. The safety, tolerability, and preliminary efficacy of two dose levels will be evaluated. The study duration is up to 6 years.

    La Jolla, California and other locations

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