Rett Syndrome clinical trials at UCSD
1 in progress, 0 open to eligible people
Sorry, not currently recruiting here
The REVEAL Pediatric Study is a multi-center, Phase 1/2 open-label, dose-escalation and dose-expansion study of TSHA-102, an investigational gene therapy, in pediatric females with Rett Syndrome. The safety, tolerability, and preliminary efficacy of two dose levels will be evaluated. The study duration is up to 6 years.
La Jolla, California and other locations