This study is in progress, not accepting new patients
A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
Summary
- Eligibility
- for males ages 8 years and up (full criteria)
- Location
- at La Jolla, California and other locations
- Dates
- study startedcompletion around
- Principal Investigator
- by Barry Greenberg, MD
Description
Summary
Official Title
Details
Keywords
Eligibility
Locations
Lead Scientist at UCSD
- Barry Greenberg, MD
Professor, Medicine, Vc-health Sciences-schools. Authored (or co-authored) 19 research publications
Details
- Status
- in progress, not accepting new patients
- Start Date
- Completion Date
- (estimated)
- Sponsor
- Rocket Pharmaceuticals Inc.
- ID
- NCT06092034
- Phase
- Phase 2 Danon Disease Research Study
- Study Type
- Interventional
- Participants
- About 12 people participating
- Last Updated